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:: Home / Scientific Program / 4° Day
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Thursday, May 12th
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THERAPEUTIC PROSPECTS IN NEUROMUSCULAR DISORDERS
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08h30
09h30
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Plenary lecture
 Jeffrey
Chamberlain
Systemic delivery of genes to striated muscle using AAV
(1h).
Moderator : Sharon Hesterlee (Grand Auditorium)
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09h30
11h00
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Parallel
symposia
"
Gene therapy and neuromuscular disorders " (1h30)
Philippe
Moullier
Gene transfer in nonhumanprimate skeletal muscle
using AAV vectors
Olivier
Danos
Gene therapies and neuromuscular diseases : the Genethon
experience
David
Klatzmann
New approaches for inflammatory muscular diseases
Jon Wolf
Naked DNA and duchenne muscular dystrophy
Moderators : Serge Braun,; Pierre Lehn (Grand Auditorium)
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Myoblast transfer and clinical applications" (1h30)
Jacques
Tremblay
Restoration of dystrophin expressions in muscle fibers of
Duchenne muscular dystrophy patients immunosuppressed with
tacrolimus
Jean
Lacau Saint-Guily
Protocol of autologous myoblast grafts in the pharyngeal
muscles to correct dysphagia in patients with OPMD
Jean-Thomas
Vilquin
Myoblast transplantation for heart failure
Christian
Pinset
Autologous cell therapy with muscle precursor cells for
stress urinary incontinence by intrinsic sphincter deficiency
: a phase I clinical trial
Moderators : Vladislav Baranov, Vincent Mouly (Amphi
800)
 11h00
- 11h45 : Break and Posters
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11h45
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Plenary lecture
Luis
Garcia
Higly efficient exon-skipping and sustained correction of
muscualr dystrophy using a Adeno-Associated Viral vector
(45mn).
Moderator : Jean-Claude Kaplan (Grand Auditorium)
12h30
: Lunch
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13h30
- 15h00 : Posters
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15h00
16h15
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Plenary
symposium
" Emerging imaging
techniques and therapies" (1h15)
 Pierre
Carlier
NMR imaging techniques and spectroscopy of the skeletal
muscle : an ever broadening spectrum of applications
Serge
Charpak
Two photon imaging and neurovascular coupling in the rat
olfactory bulb
Daniel Stockholm
Fluorescence imaging of skeletal muscle in living mice :
from organ observation to the detection of molecular activity
Moderators : François Leterrier, Michel Villaz
(Grand Auditorium)
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16h15
17h30
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Parallel symposia
" Stem cell transplantations
in muscle diseases" (1h15)
Giulio
Cossu
Mesoangioblasts, vessel associated stem cells, repair skeletal
muscle in animal models of muscular dystrophies
Yvan
Torrente
Autologous transplantation of AC133+ stem cells
in Duchenne muscular dystrophy : preclinical and clinical
evidences
Louis
Casteilla
Adipose tissue as a reservoir of therapeutic progenitors/stem
cells
Moderators : Margaret Buckingham, Romain Gherardi
(Grand Auditorium)
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Pharmacological prospects in neuromuscular
disorders " (1h15)
Arnold
Munnich
rare diseases and pharmacology : recent advances
Kate
Bushby
Can there be a consensus on the use of corticosteroids un
Duchenne muscular dystrophy ?
Kathryn
Wagner
Clinical application of myostatin inhibition
Pascal Laforêt
emerging therapies in metabolic myopathies
Moderators : Anne d'Andon, Urs Ruegg (Amphi 800)
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17h30
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Plenary lecture
Lee Sweeney
Premature stop codon suppression (1h).
Moderator : Jamel Chelly (Grand Auditorium)
20h30
: Gala Dinner
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